The MHRA is the first Regulatory body in the world to authorise a Crispr-based gene therapy. Casgevy has been authorised for patients over twelve years old who suffer from beta-thalassaemia and sickle cell disease and for whom haematopoietic stem cell transplantation is an appropriate treatment, but a suitable donor is not available. The MHRA approval sets a president in the UK, and the NHS innovative medicine fund should pave the way for eligible patients to receive a treatment for their often painful and life-threatening disease.
Casgevy
by Jackie (née Heneghan) Peck | Jan 30, 2024 | Blog, MHRA, NHS
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Testimonials
Pharmacy Consulting has been performing consultancy work for Vygon for several years, during that time they have provided us with a very professional and efficient service. PCL helped Vygon obtain their original Wholesale Dealers Licence and have provided Responsible Person (RP) support to our Quality Team ever since. PCL guided us successfully through our MHRA inspection. More recently, Jackie delivered GDP update training sessions for me and my deputy when I started in my new role as Head … Read more
Testimonial from Vygon
“Nice Chap, explained everything in an easy to understand manner!” Andrew Kruinlger – Course Rating 10/10
GDP & RP Training
“Very interactive, answered all my questions and pointers in the right direction.” Ade – Course Rating 9/10
GDP Training
“A really useful day.” Martin – Course Rating 10/10
GDP RP Training
“A relaxed training environment, and competent instructions, enabled me to gain full knowledge of what i can expect for future MHRA inspections.” David Briggs – Course Rating 9/10
GDP & RP Training
Dawn ran a very informative session about GDP guidance and the role of the Responsible Person. This helped me understand further about my role as the Responsible Person and how to stay 100% compliant according to the guidelines. I also picked up key points on what to look for when looking at potential suppliers and warehouse facilities. All together an excellent session, worth every penny! Pharmaceutical Wholesaler Client
GDP/RP Training Course
“Really enjoyed the course yesterday and felt I got a lot from attending. Knowledge will be transferable to my role, as it progresses in new areas. Material was to a high standard and Jackie was a good, knowledgeable presenter.” Export Online Training – May 2021
Export Training - May 2021
“Very clear, simple to follow. Interactive. Helpful.” Ade – Rating 9/10
Export Training
“I was a brilliant course and it opened my eyes. It gives me a platform to diversity my profile of practice.” Cogent Online Training – December 2021
Cogent (Online) - December 2021
The GPD session at PCL enabled me to focus on the really important things when it comes to getting your wholesale licence. Dawn structured the workshop in a very lively and interactive way so it is easy to follow and to use her ideas for your own business. It was very helpful, I decided to book the Audit training too.
Testimonial from Eva Böllinghaus Pharmacist of an e-pharmacy in the UK