The MHRA is the first Regulatory body in the world to authorise a Crispr-based gene therapy. Casgevy has been authorised for patients over twelve years old who suffer from beta-thalassaemia and sickle cell disease and for whom haematopoietic stem cell transplantation is an appropriate treatment, but a suitable donor is not available. The MHRA approval sets a president in the UK, and the NHS innovative medicine fund should pave the way for eligible patients to receive a treatment for their often painful and life-threatening disease.
Casgevy
by Jackie (née Heneghan) Peck | Jan 30, 2024 | Blog, MHRA, NHS
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Testimonials
“Wes was brilliant, encouraged us to be interactive and answered all the questions we posed. She was positive and patient. Fantastic trainer”
Cogent Responsible Person, December 2020
Very useful day with a good overview of MHRA GMP & GDP process, procedures and roles and responsibilities. Isatec on site training – Andrew King
GDP/RP Training
“The trainer was knowledge and answered all questions thrown at him. Training was interactive and everyone engaged. Thank you Steve for a wonderful training session.” Introduction to the RPI Role – August 2021
Intro to RPi Role - Aug 2021
Just wanted to say thank you for the training last week, was education and fun, and it was great to be able to spend time with a professional auditor.
Training Course Attendee
Waisain Al-Shamary was a lovely tutor – she allowed people to contribute and she managed a couple of strong characters with grace and patience – December 2020
Cogent Gold Standard Responsible Person Training
We contracted PCL provide us with help and guidance and training, relating to pharmaceutical transportation, we found Jackie and her team to be helpful, knowledgeable and pragmatic in their advice. The training sessions went well and were very useful in helping us understand the subject. We looked long and hard for an industry expert in this field and we certainly found one in PCL. Andrew Fox DX (Group) plc
Pharmaceutical Transportation
‘Really informative, knowledgeable and interactive. Would recommend.’ Rachel Bown
GDP/RP Training
The course covered all areas I was expecting and very well presented considering how it was delivered during the current situation. Clare Durbin 12/05/2020
Cogent Gold Standard GDP Online Training
Great training session provided by Jackie. Could consider providing additional training material (sample forms and documents) for clients apart from the GDP guidelines.
Shish from SprinBio
“Really enjoyed the training session over the last 3 days, John was a great presenter who did really well considering he had an audience from all over the UK…infact the world! I’m sure the face to face/classroom style presentation would have been more interactive as I certainly missed being able to bounce off others but this is no fault of John or the course contents. Learned so much from the past few days, more than I actually realised that I would. Thank you!” February 2021… Read more
Cogent Gold Standard Responsible Person Training